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PARIS--(BUSINESS WIRE)--Regulatory News: GenSight Biologics (Euronext : SIGHT, ISIN : FR0013183985, éligible PEA-PME), société biopharmaceutique dédiée au développement et à la commercialisation de thérapies géniques innovantes pour les maladies neurodégénératives de la rétine et les troubles du système nerveux central, publie aujourd’hui sa situation de trésorerie au 30 septembre 2026. Situation de trésorerie et programmes d’accès dérogatoires au 30 septembre 2026 La trésorerie et les équivale...

PARIS--(BUSINESS WIRE)--Regulatory News: GenSight Biologics (Euronext: SIGHT, ISIN: FR0013183985, PEA-PME eligible), a biopharma company focused on developing and commercializing innovative gene therapies for retinal neurodegenerative diseases and central nervous system disorders, today reported its cash position as of September 30, 2026. Cash Position and Early Access Programs as of September 30, 2026 GenSight Biologics’ cash and cash equivalents amounted to €0.7 million as of September 30, 20...

CRANBURY, N.J.--(BUSINESS WIRE)--Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT), a fully integrated commercial-stage biotechnology company advancing genetic medicines for rare and life-threatening diseases, highlighted key findings and development milestones presented during its October 6 Danon disease investor webinar. The update outlined a defined path to completing the FDA-aligned pivotal Phase 2 trial, highlighted sustained biological activity in longer-term Phase 1 follow-up and reported enco...

PALO ALTO, Calif. & MENLO PARK, Calif.--(BUSINESS WIRE)--Transcripta Bio, an AI-powered drug discovery company focused on neurological and neuromuscular disease, and Synfini, Inc., an agile AI foundry for small-molecule drug discovery, today announced results from a research collaboration that has produced a validated-quality lead candidate directed at MSH3, a gene increasingly understood to drive the somatic repeat expansion that paces the progression of Huntington’s disease. The companies reac...

GAITHERSBURG, Md.--(BUSINESS WIRE)--GeneDx Presents New Evidence Advancing Genomic Newborn Screening at ICoNS 2026...

AUSTIN, Texas--(BUSINESS WIRE)--Natera, Inc. (NASDAQ: NTRA), a global leader in cell-free DNA and precision medicine, today announced the enrollment of the first patients in a new Signatera-guided trial in melanoma (NCT07504796), sponsored by NYU Langone Health. The study uses Signatera to guide treatment escalation for patients with advanced or metastatic melanoma, an aggressive form of skin cancer. The current standard of care for these patients is combination immunotherapy until clinical pro...

PASADENA, Calif.--(BUSINESS WIRE)--Arrowhead Pharmaceuticals, Inc. (NASDAQ: ARWR) today announced that the United States Food and Drug Administration (FDA) has granted plozasiran entry in the Split Real Time Application Review (STAR) pilot program in connection with Arrowhead’s upcoming supplemental new drug application (sNDA) for severe hypertriglyceridemia (sHTG). SHTG is a condition that significantly increases the risk of acute pancreatitis, which is associated with repeated hospital admiss...

MONTPELLIER, France & CAMBRIDGE, Mass.--(BUSINESS WIRE)--Regulatory News: Sensorion (FR001401A9Z0 – ALSEN) (« la Société »), société de biotechnologie pionnière au stade clinique, spécialisée dans le développement de nouvelles thérapies pour restaurer l'audition et traiter et prévenir les troubles de l'audition, annonce aujourd'hui la nomination de Louis « Lou » J. Arcudi III au poste de Directeur Financier, avec effet au 7 octobre 2026. Lou Arcudi sera basé dans la région de Boston et rapporte...

MONTPELLIER, France & CAMBRIDGE, Mass.--(BUSINESS WIRE)--Regulatory News: Sensorion (FR001401A9Z0 – ALSEN) (“the Company”) a pioneering clinical-stage biotechnology company focused on developing novel therapies to restore hearing and treat and prevent hearing loss disorders, today announced the appointment of Louis “Lou” J. Arcudi III as Chief Financial Officer, effective October 7, 2026. Lou Arcudi will be based in the Boston area and will report to Fred Chereau, Chief Executive Officer. He su...

IRVINE, Calif. & AMSTERDAM--(BUSINESS WIRE)--Agendia, Inc., een toonaangevend bedrijf op het gebied van precisie-oncologie voor borstkanker, heeft vandaag aangekondigd dat het tijdens het congres van de European Society for Medical Oncology (ESMO) in 2026, dat plaatsvindt van 23 t/m 27 oktober 2026 in Madrid, nieuw onderzoek zal presenteren. Dit onderzoek betreft de ontwikkeling van een op kunstmatige intelligentie (AI) gebaseerde methode voor digitale pathologie ten behoeve van MammaPrintⓇ. Da...